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Translational enhancement by base editing of the Kozak sequence rescues haploinsufficiency

Nucleic Acids Research
2022-10-14 | Journal article
Contributors: Chiara Ambrosini; Eliana Destefanis; Eyemen Kheir; Francesca Broso; Federica Alessandrini; Sara Longhi; Nicolò Battisti; Isabella Pesce; Erik Dassi; Gianluca Petris et al.
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