Personal information

Activities

Works (2)

Twelve Years of the Gaucher Outcomes Survey (GOS): Insights, Achievements, and Lessons Learned from a Global Patient Registry

Journal of Clinical Medicine
2024-06 | Journal article | Author
Contributors: Deborah Elstein; nadia belmatoug; Bruno Bembi; Patrick Deegan; Diego Fernandez-Sasso; Pilar Giraldo; Ozlem Goker-Alpan; Derralynn Hughes; Heather Lau; Elena Lukina et al.
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Multidisciplinary Digital Publishing Institute

A Real-World Investigation of MRI Changes in Bone in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: The EIROS Study

Journal of Clinical Medicine
2024-05 | Journal article | Author
Contributors: Monia Bengherbia; Marc Berger; bénédicte HIVERT; Florian Rigaudier; Luc Bracoud; Ole Vaeterlein; Karima Yousfi; Michele Maric; Marie Malcles; nadia belmatoug
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Multidisciplinary Digital Publishing Institute

Peer review (1 review for 1 publication/grant)

Review activity for Orphanet journal of rare diseases. (1)