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A slipped-CAG DNA-binding small molecule induces trinucleotide-repeat contractions in vivo

Nature Genetics
2020-02 | Journal article
Contributors: Masayuki Nakamori; Gagan B. Panigrahi; Stella Lanni; Terence Gall-Duncan; Hideki Hayakawa; Hana Tanaka; Jennifer Luo; Takahiro Otabe; Jinxing Li; Akihiro Sakata et al.
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