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Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome

Science Translational Medicine
2024-05 | Journal article
Contributors: Giulia Consiglieri; Francesca Tucci; Maurizio De Pellegrin; Barbara Guerrini; Alessandro Cattoni; Giulia Risca; Stefano Scarparo; Marina Sarzana; Silvia Pontesilli; Renata Mellone et al.
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